Live rare diseases updates

Live rare diseases news coverage of developments with the latest updates. Stay on top of latest rare diseases news stories and find out what just happened, what is going on with rare diseases. The latest real-time news updates and headlines on rare diseases
Muscle Health Needs Lipid Synthesis
Gene Linked to X Chromosome May Explain Female’s Lower Virus Severity
Research sheds light on rare eye conditions
Research Unlocks Insights into Rare Eye Disorders
New children’s health research partnership launched in Leeds
Genome Study Targets Rare Immune Disorders in Children
Treatment Strategy Found for Bone Marrow Failure Syndrome
Cleveland Researchers Unlock Oxygen Delivery, New Drug Potential
Feature: Why rare diseases are key for scientific discovery
Shining Light on Rare Diseases and Research: Krabbe Disease
Rare Cancer Study picks out Patients at High Metastasis Risk & Those Who Will Respond to Immunotherapy
Shedding light on rare diseases: open data and model organisms
CSL’s Garadacimab Trial Yields Positive Results
Big impact of rare disease research
England to Tackle Rare Diseases Health Inequalities
Treating EoE with Single Food Omission, Not Six
Newborn Genomic Screening May Help Kids with Rare Diseases
New Chip to Aid in Vascular Malformation Research
“Data can save lives”
At Forefront: Marshaling Resources for Rare Diseases
Researchers Develop Effective Model for Leigh Syndrome Caused by Genetics
CHOP Scientists Create Effective Pre-Clinical Models for Leigh Syndrome
Toxic protein linked to muscular dystrophy and arhinia
Link Found Between Muscular Dystrophy & Arhinia: Toxic Protein
Machine Learning Boosts Genome Editing Accuracy
New Hope for Rare Brain Disorder Through Drug Reimagining
Girl Cured of Deadly Disease Using UCL Gene Therapy
High Drug Prices Unjustified Despite R&D Spending
Nonhuman Primate Model of Usher Syndrome Confirmed
Rare Neurological Disease Found by NIH Scientists
Rare Neurological Disease Linked to Cell Recycling Found by NIH
More medicines for rare diseases
Campaign Launched to Fight Rare Cancers
Research Uncovers Cause of Rare Hereditary Diseases
$25M Gift Establishes Center for Epilepsy & Neurodevelopmental
Penn Medicine Establishes Center for Epilepsy, Neurodevelopmental Disorders
Indigenous Autoimmune Liver Disease Patients Face Worse Outcomes: Study
Clinical Trials Get High-Tech Makeover with Wearables, AI
Treatment Breakthrough for Rare Metabolic Disease
Hundreds of Novel Genes Discovered in FinnGen Study
Hundreds of Novel Genetic Findings in Finland’s FinnGen Study
FinnGen Study Upends Long-Established Theories of Genetic Inheritance
HKUMed Uncovers Diagnostic Uses of Amniotic Fluid for Rare Diseases
FDA Approves Atezolizumab for Advanced Alveolar Soft Part Sarcoma
KAIST Offers Hope to Musicians with Dystonia
MHRA Gets £1m to Unlock Digital, Data & Scientific Reg Innovation
UC Davis Alpha Stem Cell Clinic receives $8 million from California’s stem cell agency
UK Government launches Newborn Genomes Programme